Results 281 to 290 of about 144,727 (384)

Understanding AAV Packaging [PDF]

Biophysical Journal, 2018
openaire   +2 more sources

Autosomal Recessive Cerebellar Ataxias: Translating Genes to Therapies

Annals of Neurology, EarlyView.
Autosomal recessive cerebellar ataxias are disabling neurodegenerative genetic conditions affecting balance and coordination. Advancements in genomic testing have improved diagnosis, leading to a new focus on the development of targeted precision therapeutics addressing cellular, biochemical, and genetic disease mechanisms with a resulting emphasis on ...
Brent L. Fogel, Thomas Klopstock, David R. Lynch, Francesca Maltecca, Mayank Verma, Berge A. Minassian, Frances M. Platt, Débora Farina Gonçalves, Hélène Puccio, Andreas Roos, Matthis Synofzik   +10 more
wiley   +1 more source

Hydralazine-Induced ANCA-Associated Vasculitis With Lupus Nephritis Features and a Unique Antibody Profile. [PDF]

J Community Hosp Intern Med Perspect
Rabie M, Scalise M.
europepmc   +1 more source

Mechanochemical Strategies Applied to the Late‐Stage Modifications of Pharmaceutically Active Compounds

Angewandte Chemie International Edition, Accepted Article.
This review explores the potential of mechanochemistry in the late‐stage modification of active pharmaceutical ingredients (APIs), offering a comprehensive analysis of methods designed to transform structurally complex molecular scaffolds. By examining the scope, efficiency, and mechanistic aspects of these approaches, the review highlights protocols ...
Johanna Templ, Lars Borchardt
wiley   +1 more source

AAV-Mediated Expression of Methamphetamine Monoclonal Antibody Attenuates Methamphetamine Behaviour Sensitization in Mice. [PDF]

Addict Biol
Chen YH, Hung TW, Wang YS, Bae EK, Wu KJ, Wang Y, Yu SJ.   +6 more
europepmc   +1 more source

136. Effective Delivery of AAV to the Liver Via Retrograde Infusion of the Biliary Tree [PDF]

, 2002

openalex   +1 more source

Clinical Factors Associated With Pneumocystis Pneumonia Despite Its Primary Prophylaxis: When to Stop Prophylaxis?

Arthritis &Rheumatology, EarlyView.
Objective Although previous studies show that primary prophylaxis against Pneumocystis jirovecii pneumonia (PJP) is effective in patients with rheumatic diseases receiving immunosuppressive treatment, there is limited evidence regarding the optimal timing for prophylaxis withdrawal.
Ju Yeon Kim, Se Rim Choi, Jin Kyun Park, Eun Young Lee, Eun Bong Lee, Jun Won Park   +5 more
wiley   +1 more source

Retinal Epithelial Neutralization Assay Optimizes AAV Serotype Selection for Ocular Gene Therapy. [PDF]

Viruses
Li Y, Chen Y, Huo N, Jia Z, Huang H, Zhao Z, Wu S, Hou L.   +7 more
europepmc   +1 more source

251. Creation and Characterization of High Titer AAV-Factor IX Producing Clones for Clinical Scale Production [PDF]

, 2002

openalex   +1 more source

AAV Entry: Filling in the Blanks [PDF]

Molecular Therapy, 2020
openaire   +2 more sources