Results 101 to 110 of about 6,507 (124)

AAV-mediated transgene delivery targeting spiral ganglion nonsensory cells. [PDF]

Neuroreport
Lin JS, Nguyen NV, Shibata SB.
europepmc   +1 more source

Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in <i>Epm2b</i>-Deficient Mice. [PDF]

Int J Mol Sci
Zafra-Puerta L, Iglesias-Cabeza N, Sanz P, García-Gimeno MA, Sánchez-Martín G, Sánchez MP, Serratosa JM.   +6 more
europepmc   +1 more source

Successful in vitro propagation of porcine bocavirus: Demonstrating dual respiratory-enteric tropism and pathogenicity. [PDF]

PLoS Pathog
Ji Z, Zhang X, Xue M, Chen J, Shi D, Shi H, Zhang H, Zhang L, Feng T, Zhu X, Li X, Liu D, Wang M, Zeng M, Feng L.   +14 more
europepmc   +1 more source

Subretinal Injection Volume Correlates to Persistent Outer Retinal Thinning in the Pig Eye. [PDF]

Invest Ophthalmol Vis Sci
Seitz IP, Nyshchuk R, Ellederova Z, Ardan T, Juhasova J, Nemesh Y, Juhas S, Drutovic S, Süsskind D, Schnichels S, Motlik J, Klymiuk N, Wolfrum U, Post DeMott K, Klein JJ, Winslow A, Fischer MD.   +16 more
europepmc   +1 more source

Dystrophin/mini-dystrophin expression analysis by immunoaffinity liquid chromatography-tandem mass spectrometry after gene therapy for DMD. [PDF]

Gene Ther
Walsh J, Palandra J, Duriga N, Beidler D, McIntosh A, Binks M, Neubert H.   +6 more
europepmc   +1 more source

ShH10 viral vector for safe, efficient, and selective transduction of inner ear supporting cells. [PDF]

Dev Biol
Bertken YJ, Kim Y, Llamas J, Beck A, Nagiel A, Gnedeva K.   +5 more
europepmc   +1 more source

A Novel Role for the Adenovirus L4 Region 22K and 33K Proteins in Adeno-Associated Virus Production. [PDF]

Hum Gene Ther
Adsero A, Chestnut B, Shahnejat-Bushehri S, Sasnoor L, McMurphy T, Swenor M, Pasquino R, Pradhan A, Hernandez V, Padegimas L, Dismuke D.   +10 more
europepmc   +1 more source

Gene therapy for hemophilia B: results from the phase 1/2 101HEMB01/02 studies. [PDF]

Blood Adv
Pipe S, Poma A, Rajasekhar A, Everington T, Sankoh S, Allen J, Cataldo J, Crombez E.   +7 more
europepmc   +1 more source

Protocol for detecting LDLR on the cell surface of primary mouse hepatocytes using cell-surface biotinylation. [PDF]

STAR Protoc
Ma F, Cai B.
europepmc   +1 more source

When size matters: A novel compact Cas12a variant for in vivo genome editing. [PDF]

PLoS Biol
Bubeck F, Grimm D.
europepmc   +1 more source