Results 101 to 110 of about 6,602 (127)

AAV9-mediated transduction of memory circuits following convection-enhanced delivery into the olfactory bulbs. [PDF]

Gene Ther
Dimitrov T, Munjal V, O'Brien A, Rocco MT, Karkhah A, Ceyhan KE, Prevedello D, Samaranch L.   +7 more
europepmc   +1 more source

Pre-existing Anti-AAV9 antibodies in the Chinese healthy and rare disease populations: Implications for gene therapy. [PDF]

Virus Res
Zhao Q, Yu S, Fu D, Wu Z, Zhou J, Yang Y, Chen C, Wu N, Wang Y, Xi W, Lou N, Wu X, Han X.   +12 more
europepmc   +1 more source

Tunable dual-AAV sparse labeling of PV⁺ retinal ganglion cells enables single-neuron projection by fMOST. [PDF]

Front Neural Circuits
Zhou L, Tan G, Li Y, Yuan M, Jin S, Zhang W, Wang Q, Shen Y.   +7 more
europepmc   +1 more source

Neo-antigen tumor vaccination depends on CD4-licensing conveyed by adeno-associated virus like particles. [PDF]

Mol Ther
Neukirch L, Uhrig-Schmidt S, von Werthern K, Tuch A, Kraske JA, Lyu Y, Lenoir B, Eichmüller SB, Meyer M, Zörnig I, Jäger D, Schmidt P.   +11 more
europepmc   +1 more source

Rationale and design of MUSIC-HFpEF: a phase 1b, pilot trial evaluating the safety and pharmacodynamic effects of AAV1.SERCA2A in heart failure with preserved ejection fraction. [PDF]

Heart Fail Rev
Fudim M, Sarma S, MacNamara JP, Ascheim DD, Kittipibul V, Doukellis K, Dhimitri A, Fitzhugh R, Kamat N, Costa KD, Rudy J, Guerrero J, Chan C, Li RA, Bavry AA, Patel MR, Grodin JL, Levine BD, Hajjar RJ.   +18 more
europepmc   +1 more source

Real-world outcomes of delandistrogene moxeparvovec gene therapy: Motor outcomes and emerging safety concerns. [PDF]

Mol Ther
Keselman DJ, Small JC, Seneviratne T, McCague S, Kaschak TL, Yum SW, O'Brien A, Brandsema JF, Diamond T, Loomes KM, Lin KY, Wittlieb-Weber CA, Mayer OH, Daniel SG, Waldman AT, Samelson-Jones BJ, Matesanz SE, George LA.   +17 more
europepmc   +1 more source

Streamlining mouse genome editing by integrating AAV repair template delivery and CRISPR-Cas electroporation. [PDF]

Lab Anim (NY)
Moncaut N.
europepmc   +1 more source

Retinal Epithelial Neutralization Assay Optimizes AAV Serotype Selection for Ocular Gene Therapy. [PDF]

Viruses
Li Y, Chen Y, Huo N, Jia Z, Huang H, Zhao Z, Wu S, Hou L.   +7 more
europepmc   +1 more source

Podocyte-directed VEGFC gene therapy prevents increased glomerular permeability and glycocalyx damage in experimental type 1 diabetes. [PDF]

Mol Ther
Martin Alonso A, May CJ, Stowell-Connolly H, Wu H, Gamez M, Ourradi K, Ramnath RD, Ding WY, Welsh GI, Satchell SC, Foster RR.   +10 more
europepmc   +1 more source

CapBuild: a cloud-native tool for adeno-associated virus capsid engineering. [PDF]

Nucleic Acids Res
Klein AH, Kuiper MJ, Burgess M, Wickramarachchi A, Jain Y, Bauer DC, Wilson L.   +6 more
europepmc   +1 more source