Frameless intraputaminal delivery of gene therapy with eladocagene exuparvovec in patients with aromatic L-amino acid decarboxylase deficiency: safe and efficient results. [PDF]
Childs Nerv SystMai R +5 more
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An Expanded Toolbox for Versatile Chemical Editing of Adeno-Associated Virus. [PDF]
Angew Chem Int Ed EnglPham Q +6 more
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Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in Mice. [PDF]
CellsZhang J +9 more
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Species barriers in AAV tropism: mechanisms, models, and emerging solutions for clinical translation. [PDF]
Acta Biochim PolXu X.
europepmc +1 more source
Functional Evaluation of Computationally Designed IL-10 in IL-10 KO Mice. [PDF]
BiomoleculesStokes J +7 more
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Development and Preliminary Application of a Beak Development Index in Pathogenicity Studies of Novel Goose Parvovirus. [PDF]
Vet SciShao Y +8 more
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AAV2-Retro-Mediated Gene Transfer Selectively Targets Outer Retinal Cells Following Intravitreal Injection. [PDF]
Invest Ophthalmol Vis SciKinane C +4 more
europepmc +1 more source
Quantitative Analysis and Predictive Modeling of Nonspecific Adsorption of Recombinant Adeno-Associated Virus onto Solid Surfaces. [PDF]
LangmuirUeda Y +6 more
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Systemic AAV9 Gene Therapy Mitigates Neuromuscular Junction Degeneration and Muscle Atrophy in a Mouse Model of CLN1 Disease. [PDF]
Int J Mol SciZiółkowska EA +8 more
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A Novel Strategy to Produce CAR-γδ T Cells via Site-Directed Gene Integration by a Combination of CRISPR/Cas9 and AAV. [PDF]
Cancer MedDong R +6 more
europepmc +1 more source