Results 111 to 120 of about 6,673 (141)

Streamlining mouse genome editing by integrating AAV repair template delivery and CRISPR-Cas electroporation. [PDF]

Lab Anim (NY)
Moncaut N.
europepmc   +1 more source

Efficacy and Safety of Gene Therapy for RPGR Gene-Associated X-Linked Retinitis Pigmentosa: A Systematic Review and Meta-Analysis. [PDF]

Transl Vis Sci Technol
Yang J, Lei Y, Xiao B, Li Y, Lai D, Qiu Q.   +5 more
europepmc   +1 more source

AAV2.7m8-Mediated MicroRNA Expression Suppresses VEGF-Induced Angiogenic Responses in HUVEC. [PDF]

Int J Mol Sci
Yang JY, Choi JS, Park TK.
europepmc   +1 more source

Neo-antigen tumor vaccination depends on CD4-licensing conveyed by adeno-associated virus like particles. [PDF]

Mol Ther
Neukirch L, Uhrig-Schmidt S, von Werthern K, Tuch A, Kraske JA, Lyu Y, Lenoir B, Eichmüller SB, Meyer M, Zörnig I, Jäger D, Schmidt P.   +11 more
europepmc   +1 more source

Performance of large virus removal filters during AAV processing: Influence of flux and process disruptions. [PDF]

Biotechnol Prog
Chaubal AS, Arachchige AW, Zahn AJ, Wickramasinghe SR, Qian X, Zydney AL.   +5 more
europepmc   +1 more source

Rationale and design of MUSIC-HFpEF: a phase 1b, pilot trial evaluating the safety and pharmacodynamic effects of AAV1.SERCA2A in heart failure with preserved ejection fraction. [PDF]

Heart Fail Rev
Fudim M, Sarma S, MacNamara JP, Ascheim DD, Kittipibul V, Doukellis K, Dhimitri A, Fitzhugh R, Kamat N, Costa KD, Rudy J, Guerrero J, Chan C, Li RA, Bavry AA, Patel MR, Grodin JL, Levine BD, Hajjar RJ.   +18 more
europepmc   +1 more source

Retinal Epithelial Neutralization Assay Optimizes AAV Serotype Selection for Ocular Gene Therapy. [PDF]

Viruses
Li Y, Chen Y, Huo N, Jia Z, Huang H, Zhao Z, Wu S, Hou L.   +7 more
europepmc   +1 more source

Tunable dual-AAV sparse labeling of PV⁺ retinal ganglion cells enables single-neuron projection by fMOST. [PDF]

Front Neural Circuits
Zhou L, Tan G, Li Y, Yuan M, Jin S, Zhang W, Wang Q, Shen Y.   +7 more
europepmc   +1 more source

Incidence, timing, and clinical significance of adverse immune events after gene replacement therapy: A systematic review and meta-analysis. [PDF]

Mol Ther
Maurizi N, Ammirati E, Silver E, Hong K, Bui Q, Argirò A, Olivotto I, Adler ED.   +7 more
europepmc   +1 more source