Results 81 to 90 of about 6,270 (121)

Considerations for the Use of AAV-based Gene Therapy in HIV-Positive Individuals With Haemophilia. [PDF]

Haemophilia
Rockstroh JK, Stingl JC, Stadler M, Reichert A, Wedemeyer H, Oldenburg J.   +5 more
europepmc   +1 more source

Mass Determination of Filled and Empty AAV5 Particles Enabled by Nanoelectrospray Ionization and Proton Transfer Charge Reduction. [PDF]

Anal Chem
Pizzala NJ, Faye BKS, Song H, Tao L, McLuckey SA.   +4 more
europepmc   +1 more source

T2 Hyperintensities in Gracile Tracts of Cervical Spinal Cord in Giant Axonal Neuropathy (GAN). [PDF]

Muscle Nerve
Armao D, Bouldin TW, Bharucha-Goebel DX, Hartman TS, Gray SJ, Bailey RM, Saade D, Todd JJ, Jain M, Waite M, Bönnemann CG, Smith JK.   +11 more
europepmc   +1 more source

Recombinant adeno-associated virus 2-mediated miRNA-199 suppression vector alleviates dextran sulfate sodium-induced ulcerative colitis in mice. [PDF]

Virus Res
Shanshan W, Yu Z.
europepmc   +1 more source

Advances in endothelial cell targeting by AAV vectors. [PDF]

Acta Biochim Pol
Cichon M, Jozkowicz A, Grochot-Przeczek A.   +2 more
europepmc   +1 more source

Monitoring Fetal Somatic Cell Genome Editing <i>In Vivo</i> with Total-Body Positron Emission Tomography: Studies in Rhesus Macaques (<i>Macaca mulatta</i>). [PDF]

Hum Gene Ther
Tarantal AF, Martinez ML, Sanz L, Lee CI, Yang H, O'Geen H, Hartigan-O'Connor DJ, Segal DJ.   +7 more
europepmc   +1 more source

Gene-replacement therapy in neurodevelopmental disorders: progress and challenges. [PDF]

J Clin Invest
Lerche H, Hedrich UB, Wuttke TV.
europepmc   +1 more source

Identification of Recombinant Adeno-Associated Virus Serotypes by Matrix-Assisted Laser Desorption/Ionization Mass Spectrometry. [PDF]

Anal Chem
Nakatsuka R, Matsumoto K, Liu Y, Takeda K, Tsunaka Y, Torisu T, Yamaguchi Y, Uchiyama S.   +7 more
europepmc   +1 more source

Triple rAAV9 Vector Combinations Encoding Broadly Neutralizing Antibodies Effectively Suppress HIV-1 Infection in Humanized Mice. [PDF]

Int J Mol Sci
Leontyev DS, Urusov FA, Glazkova DV, Belugin BV, Mitiushina AA, Tsyganova GM, Yudin SM, Bogoslovskaya EV, Shipulin GA.   +8 more
europepmc   +1 more source

Metadata assessment of non-human primate studies of AAV9 uncovers potential tissue specific variation in expression efficiency. [PDF]

Gene Ther
Shahrukh M, Sweeney JR, Del Rio T, Ozsolak F.   +3 more
europepmc   +1 more source