Gene augmentation therapy successfully treats mice with complete congenital stationary night blindness (cCSNB), improving retinal function and visual acuity. [PDF]
Gene TherHasan N +4 more
europepmc +1 more source
Aiming for spatial and temporal control of gene expression. [PDF]
ElifeIgor Travisano S, Lien CL.
europepmc +1 more source
Determination of AAV Capsid Protein Ratios by Sodium Dodecyl Sulfate Capillary Electrophoresis (CE-SDS)-UV Absorption Method. [PDF]
ElectrophoresisLi Y +10 more
europepmc +1 more source
Efficient Endolymphatic Sac-Directed Gene Delivery Using AAV8BP2 and Posterior Semicircular Canal Injection. [PDF]
Int J Mol SciKang M +4 more
europepmc +1 more source
High resolution ES-DMA quantifies AAV capsid DNA content by electrical mobility to mass correlation. [PDF]
Gene TherDennett P +5 more
europepmc +1 more source
AAV2 capsid clearance and neuronal trafficking dynamics in the central nervous system. [PDF]
Gene TherGullapalli T +11 more
europepmc +1 more source
Could AAV-vectored delivery of broadly neutralizing antibodies (bNAbs) reduce virologic failure in children diagnosed with perinatal HIV? [PDF]
Hum Vaccin ImmunotherPringle KL, Martins MA.
europepmc +1 more source
mGem: AAV, from almost a virus to an awesome vector-or is it? [PDF]
mBioSrivastava A.
europepmc +1 more source
Steering Protein Generative Models at Test-Time for Guided AAV2 Capsid Design. [PDF]
Pac Symp BiocomputViggiano B +6 more
europepmc +1 more source
EctoShed: a novel gene delivery platform for functional analysis of adipocyte-shed proteoforms. [PDF]
BMC Res NotesTavanez AR +4 more
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