Optimization of viral transduction in the central nervous system [PDF]
, 2016 Genetically based Central Nervous System (CNS) disorders remain a largely unresolved issue in the world today. Our genome is the source of our greatest strengths and weaknesses.
Burt, Daniel Robert
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General Information on the Vertebrate Virus Data Bank "DAISY" [PDF]
, 1984 Bachmann, P. A., Eichhorn, Werner
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Continuous cell lines from the Muscovy duck as potential replacement for primary cells in the production of avian vaccines [PDF]
, 2016 Gubucz-Sombor, Erzsébet +6 more
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Aiming for spatial and temporal control of gene expression. [PDF]
ElifeIgor Travisano S, Lien CL.
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The calcium awakens: new insights in cardiac gene therapy. [PDF]
Front Endocrinol (Lausanne)Santulli G.
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First-in-human study of TN-201, an AAV9 gene replacement therapy in MYBPC3-associated hypertrophic cardiomyopathy: initial safety, pharmacodynamic, and imaging results from MyPEAK-1. [PDF]
Cardiovasc ResDesai MY +17 more
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Pervasive horizontal transfer of adeno-associated virus capsid genes. [PDF]
Proc Natl Acad Sci U S AGifford RJ.
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Compact Calm1 promoter enables AAV mediated neuron-targeted expression in human iPSC-derived brain organoids. [PDF]
Sci RepKlockner I +4 more
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The Impact of QSP Modeling on the Design and Optimization of Gene Therapy Approaches. [PDF]
CPT Pharmacometrics Syst PharmacolRayad N, Chowdhury EA, Meno-Tetang GML.
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