Results 151 to 160 of about 56,717 (273)

A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells.

open access: yesCell Stem Cell, 2016
C. Young   +17 more
semanticscholar   +1 more source

Dystrophin and the brain [PDF]

open access: yesDevelopmental Medicine & Child Neurology, 2010
Ricotti, Valeria   +2 more
openaire   +3 more sources

In Vivo Genome Editing Restores Dystrophin Expression and Cardiac Function in Dystrophic Mice

open access: yesCirculation Research, 2017
Mona El Refaey   +11 more
semanticscholar   +1 more source

Emerging roles of microRNAs and other non-coding transcriptome in muscular dystrophies. [PDF]

open access: yesInflamm Regen
Abdelrehim FG   +5 more
europepmc   +1 more source

Duchenne Muscular Dystrophy: Contemporary Therapeutic Options and Real-World Challenges in Treatment Selection. [PDF]

open access: yesMuscles
Pesco MT   +5 more
europepmc   +1 more source

The role of chromosome territories in the funtional compartmentalization of the cell nucleus [PDF]

open access: yes, 1993
Cremer, Christoph   +13 more
core   +1 more source

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