Molecular Mechanisms and Therapeutic Strategies in Heart Failure Due to Dystrophin Deficiency: A Comprehensive Review. [PDF]
Yu W, Wang W, Luo F, Zhao Y, Wu Q, Li P.
europepmc +1 more source
YAP Acts as a Negative Regulator of Mini Utrophin-Based Gene Therapy for Duchenne Muscular Dystrophy in Mdx Mice. [PDF]
Li Z, Song Y.
europepmc +1 more source
Emerging roles of microRNAs and other non-coding transcriptome in muscular dystrophies. [PDF]
Abdelrehim FG +5 more
europepmc +1 more source
Duchenne Muscular Dystrophy: Contemporary Therapeutic Options and Real-World Challenges in Treatment Selection. [PDF]
Pesco MT +5 more
europepmc +1 more source
Viscoelastic properties of dystrophin-deficient mouse skeletal muscles are resilient to isometric fatiguing exercise. [PDF]
Merry DL +3 more
europepmc +1 more source
Nicotinamide and Pyridoxine Supplementation Enhances Muscle Stem Cell Activity and Muscle Regeneration in Humans: A Randomized Placebo-Controlled Clinical Trial of High Force Eccentric Contraction Recovery in Healthy Young Men. [PDF]
Højfeldt G +14 more
europepmc +1 more source
RNA Therapeutics for Duchenne Muscular Dystrophy: Exon Skipping, RNA Editing, and Translational Insights from Genome-Edited Microminipig Models. [PDF]
Chassin A +4 more
europepmc +1 more source
Dystrophin-Deficient Cardiomyopathy Due to a Novel Hemizygous DMD Indel Variant. [PDF]
Albrecht K +8 more
europepmc +1 more source
Bioengineered AAV9 and Optimised Microdystrophin Vectors Augment Phenotypic Rescue in a Murine Model of Duchenne Muscular Dystrophy. [PDF]
Senthilkumar MB +14 more
europepmc +1 more source
Preclinical evaluation of INS1201 AAV9-micro-dystrophin via CSF administration as a potential therapy for Duchenne muscular dystrophy. [PDF]
Thomsen G +35 more
europepmc +1 more source

