Results 161 to 170 of about 21,009 (196)

Human dystrophin gene transfer: genetic correction of dystrophin deficiency

1993
Somatic gene therapy, as generally conceived, involves reconstituting a biological function by adding a normal gene to somatic, i.e. non-germline, cells which are genetically deficient in that gene product (Friedmann, 1989). Single gene or Mendelian disorders which are recessive (autosomal or X-linked) are particularly attractive candidates for such a ...
G, Dickson, M, Dunckley
openaire   +2 more sources

Dystrophin digest

Nature, 1989
K, Arahata, S, Ishiura, T, Tsukahara, H, Sugita   +3 more
openaire   +2 more sources

Hippocampal LTP in dystrophin and dystrophin isoforms deficient mice.

1997
info:eu-repo/semantics ...
Godfraind, J M, Zizi, Martin, Deconinck, Nicolas   +2 more
openaire   +2 more sources

Dystrophin

Neurology, 1992
Kiichi Arahata, Eric P. Hoffman
openaire   +2 more sources

Dystrophin

The Lancet, 1988
  +5 more sources

Dystrophin and Dystrophin-Associated Proteins

2014
I. Kleyman, T.H. Brannagan
openaire   +1 more source

Dystrophin and the Retina

Molecular Genetics and Metabolism, 1999
openaire   +2 more sources

Dystrophin Gene-Editing Stability Is Dependent on Dystrophin Levels in Skeletal but Not Cardiac Muscles

Molecular Therapy, 2021
Jeffrey Chamberlain, Niclas Bengtsson, Hichem Tasfaout   +2 more
exaly  

Dystrophin and Dystrophin-Associated Proteins

2003
openaire   +1 more source

Dystrophin and Duchenne dystrophy

Neuromuscular Disorders, 2015
Victor, Dubowitz, Ronald D, Cohn
openaire   +2 more sources