Results 171 to 180 of about 28,350 (246)

Successful In Vitro Modification of the <i>Dmd</i> Gene Using Prime Editing. [PDF]

Cells
Siddika A, Husseiny FE, Rousseau J, Tremblay JP.   +3 more
europepmc   +1 more source

Adeno-Associated Virus Toxicity in Duchenne Muscular Dystrophy: Mechanisms and Clinical Considerations. [PDF]

Genes (Basel)
Saylam E, D'ambrosio ES, Pesco MT, Gushchina LV.   +3 more
europepmc   +1 more source

Optical coherence tomography findings in Duchenne muscular dystrophy. [PDF]

BMC Ophthalmol
Yöyler G, Adıyeke SK.
europepmc   +1 more source

Mutation of leucine 170 alters the subcellular distribution, neurite outgrowth and three-dimensional structure of dystrophins Dp71 and Dp40. [PDF]

Mol Biol Rep
García-Cruz C, Sanchez-Perez L, Herrera-Rojas F, Posadas-Trejo M, Ceja V, Sánchez-Trujillo A, Merino-Jiménez C, Aragón J, Montanez C.   +8 more
europepmc   +1 more source

Correction: The rise of rat models for Duchenne muscular dystrophy and therapeutic evaluations. [PDF]

Skelet Muscle
Relaix F, Lafuste P, Taglietti V, Tiret L.   +3 more
europepmc   +1 more source

State-of-the-Art Research and New Pharmacological Perspectives on Renal Involvement in Duchenne Muscular Dystrophy: A Narrative Review. [PDF]

Biomedicines
Bellis M, Imbrici P, Lenti R, Liantonio A, De Luca A.   +4 more
europepmc   +1 more source

Molecular Bases of Myopathies and Their Impact on Clinical Practice: Advances and Future Perspectives. [PDF]

Int J Mol Sci
Campuzano-Donoso M, Reytor-González C, Toral-Noristz M, González Y, Simancas-Racines D.   +4 more
europepmc   +1 more source

PPMO-based exon skipping therapy improves respiratory function in the <i>mdx</i> mouse model of Duchenne muscular dystrophy. [PDF]

Mol Ther Nucleic Acids
Biswas DD, Rodriguez MYH, El Haddad L, Hoffmann G, Copson E, Mayman S, Jose J, Lang S, Chen O, Dela Pena A, Levin E, Abdelbarr M, Slyne A, ElMallah MK.   +13 more
europepmc   +1 more source

Proteomics-based evaluation of AAV dystrophin gene therapy outcomes in mdx skeletal muscle. [PDF]

JCI Insight
Johnson EE, Reyes TR, Chamberlain JS, Ervasti JM, Tasfaout H.   +4 more
europepmc   +1 more source

Improving angiogenesis ameliorates the efficacy of ASO-based exon skipping for the treatment of Duchenne muscular dystrophy. [PDF]

Mol Ther Nucleic Acids
Blitek M, Gastaldi C, Doisy M, Le Coz O, David M, Phongsavanh X, Ben Aicha S, Garcia L, Rotini A, Pagès G, Goyenvalle A.   +10 more
europepmc   +1 more source