Results 171 to 180 of about 56,717 (273)

Dystrophin rescue in the brain for DMD. [PDF]

Mol Ther Nucleic Acids
Li M, Han R.
europepmc   +1 more source

Adeno-Associated Virus Toxicity in Duchenne Muscular Dystrophy: Mechanisms and Clinical Considerations. [PDF]

Genes (Basel)
Saylam E, D'ambrosio ES, Pesco MT, Gushchina LV.   +3 more
europepmc   +1 more source

Dual AAV Gene Therapy for Duchenne Muscular Dystrophy with a 7-kb Mini-Dystrophin Gene in the Canine Model

Human Gene Therapy, 2017
Kasun Kodippili, Chady H. Hakim, Xiufang Pan, Hsiao T. Yang, Y. Yue, Yadong Zhang, Jin-Hong Shin, N. N. Yang, D. Duan   +8 more
semanticscholar   +1 more source

Mutation of leucine 170 alters the subcellular distribution, neurite outgrowth and three-dimensional structure of dystrophins Dp71 and Dp40. [PDF]

Mol Biol Rep
García-Cruz C, Sanchez-Perez L, Herrera-Rojas F, Posadas-Trejo M, Ceja V, Sánchez-Trujillo A, Merino-Jiménez C, Aragón J, Montanez C.   +8 more
europepmc   +1 more source

Correction: The rise of rat models for Duchenne muscular dystrophy and therapeutic evaluations. [PDF]

Skelet Muscle
Relaix F, Lafuste P, Taglietti V, Tiret L.   +3 more
europepmc   +1 more source

State-of-the-Art Research and New Pharmacological Perspectives on Renal Involvement in Duchenne Muscular Dystrophy: A Narrative Review. [PDF]

Biomedicines
Bellis M, Imbrici P, Lenti R, Liantonio A, De Luca A.   +4 more
europepmc   +1 more source

Dystrophin and Its Isoforms

Brain Pathology, 1996
H M, Sadoulet-Puccio, L M, Kunkel
openaire   +2 more sources

PPMO-based exon skipping therapy improves respiratory function in the <i>mdx</i> mouse model of Duchenne muscular dystrophy. [PDF]

Mol Ther Nucleic Acids
Biswas DD, Rodriguez MYH, El Haddad L, Hoffmann G, Copson E, Mayman S, Jose J, Lang S, Chen O, Dela Pena A, Levin E, Abdelbarr M, Slyne A, ElMallah MK.   +13 more
europepmc   +1 more source

Molecular Bases of Myopathies and Their Impact on Clinical Practice: Advances and Future Perspectives. [PDF]

Int J Mol Sci
Campuzano-Donoso M, Reytor-González C, Toral-Noristz M, González Y, Simancas-Racines D.   +4 more
europepmc   +1 more source

Proteomics-based evaluation of AAV dystrophin gene therapy outcomes in mdx skeletal muscle. [PDF]

JCI Insight
Johnson EE, Reyes TR, Chamberlain JS, Ervasti JM, Tasfaout H.   +4 more
europepmc   +1 more source