Systemic MyoAAV-saRNA delivery activates endogenous utrophin and rescues dystrophic pathology in mdx mice. [PDF]
Xiahou Z +8 more
europepmc +1 more source
Using muscle homing peptide CyPep10 to deliver phosphorodiamidate morpholino oligomers in the mdx mouse. [PDF]
Schneider AE +11 more
europepmc +1 more source
Longitudinal Changes of Motor Function in Becker Muscular Dystrophy. [PDF]
Bello L +13 more
europepmc +1 more source
Ubiquitination-targeted therapies improve BMD iPSC myogenic cell engraftment and dystrophin expression <i>in vivo</i>. [PDF]
Liu M +6 more
europepmc +1 more source
Duchenne Muscular Dystrophy: Integrating Current Clinical Practice with Future Therapeutic and Diagnostic Horizons. [PDF]
Montagna C +3 more
europepmc +1 more source
Interaction of dystrophin fragments with model membranes
Christine DeWolf +7 more
openalex +1 more source
Brogidirsen and Exon 44 Skipping for Duchenne Muscular Dystrophy: Advances and Challenges in RNA-Based Therapy. [PDF]
Tang A, Yokota T, Yokota T.
europepmc +1 more source
Dystrophin‐deficiency increases the susceptibility to doxorubicin‐induced cardiotoxicity
Shiwei Deng +6 more
openalex +2 more sources

