Results 281 to 290 of about 8,657,992 (314)

CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia

Nature Medicine, 2022
Bin Fu, Jiaoyang Liao, Shuanghong Chen, Wei Li, Qiudao Wang, Jian Hu, Fei Yang, Shenlin Hsiao, Yang-kai Jiang, Liren Wang, Fangping Chen, Yuanjin Zhang, Xin Wang, Dali Li, Ming-Yu Liu, Yuxuan Wu   +15 more
semanticscholar   +1 more source

Gene Therapy and Gene Editing

2023
Basel T. Assaf, Claudia Harper, Jonathan A. Phillips   +2 more
openaire   +1 more source

Nanobiomaterial vectors for improving gene editing and gene therapy

Materials Today, 2023
Shao Wei Hu, Tao Ding, Honghai Tang
exaly  

Lipid Nanoparticle-Mediated Hit-and-Run Approaches Yield Efficient and Safe In Situ Gene Editing in Human Skin

ACS Nano, 2023
Davide Brambilla, Pieter R Cullis, Sarah Hedtrich   +2 more
exaly  

CRISPR-GPT: An LLM Agent for Automated Design of Gene-Editing Experiments

arXiv.org
Kaixuan Huang, Yuanhao Qu, H. Cousins, William A. Johnson, Di Yin, Mihir M. Shah, Denny Zhou, Russ B. Altman, Mengdi Wang, Le Cong   +9 more
semanticscholar   +1 more source

Gene Editing

2021
openaire   +1 more source

A Versatile Nonviral Delivery System for Multiplex Gene‐Editing in the Liver

Advanced Materials, 2020
Jing Gong, Hong-Xia Wang, Yeh-Hsing Lao   +2 more
exaly  

Hematopoietic Stem Cell-Targeted Gene-Addition and Gene-Editing Strategies for β-hemoglobinopathies

Cell Stem Cell, 2021
Tina Nassehi, Jackson Gamer, Morgan Yapundich   +2 more
exaly  

RNA-targeting and gene editing therapies for transthyretin amyloidosis

Nature Reviews Cardiology, 2022
Alberto Aimo, V. Castiglione, C. Rapezzi, M. Franzini, G. Panichella, G. Vergaro, J. Gillmore, M. Fontana, C. Passino, M. Emdin   +9 more
semanticscholar   +1 more source

Plant gene editing improved

Nature Reviews Molecular Cell Biology, 2019
Kim Baumann, Baumann Kim
exaly