Results 291 to 293 of about 172,174 (293)

EVALUATING GENE REPLACEMENT THERAPY FOR CTNNB1 HAPLOINSUFFICIENCY

Cytotherapy
L.W. Tessier, J. Alexander, M. Jacob
openaire   +1 more source

From Clinical Trials to Clinical Practice: Practical Considerations for Gene Replacement Therapy in SMA Type 1

Pediatric Neurology, 2019
exaly  

Erratum to: Viral Vectors in Gene Replacement Therapy

Biochemistry (Moscow)
Ekaterina Minskaia, Alima Galieva, Alexander D. Egorov, Roman Ivanov, Alexander Karabelsky   +4 more
openaire   +1 more source