High-titer modular retroviral vectors enabled by an antisense cassette design preventing dsRNA formation during virus production. [PDF]
Vuillefroy de Silly R +2 more
europepmc +1 more source
Reduced <i>LINC01089</i> Expression Impairs Coordinated Heme-Globin Transcriptional Programs in Human Erythroid Cells. [PDF]
Xue Y, Li X, Zhang Y, Ma F.
europepmc +1 more source
miRNA-Mediated Regulation of γ-Globin to β-Globin Switching: Therapeutic Potential in β-Hemoglobinopathies. [PDF]
Alotaibi D +11 more
europepmc +1 more source
Correction: Genotypic and phenotypic characterization of rare globin variants in Northern Guangxi, China. [PDF]
Yang WJ +7 more
europepmc +1 more source
A novel polyadenylation signal variant NM_000517.6 (<i>HBA2</i>): c.*92_*97delinsTA causing α-thalassemia in two Chinese families. [PDF]
Huang W +6 more
europepmc +1 more source
Hemoglobin alpha-like subunit mu is expressed during ontogeny and is elevated in alpha thalassemia. [PDF]
Garapati K +8 more
europepmc +1 more source
Clinical Trial Landscape of Gene-Edited Autologous Hematopoietic Stem Cells for Hemoglobinopathies and Immunodeficiencies. [PDF]
O'Hanlon Cohrt K, O'Dea S.
europepmc +1 more source
Rare Case Report of Hb J Meerut Hemoglobinopathy - a Hospital Insight in the Saurashtra-Kutch Region of Gujarat. [PDF]
Anandani G +4 more
europepmc +1 more source
Highly discriminative globin gene activation by the noncanonical BAF chromatin remodeling complex. [PDF]
Bagchi A +15 more
europepmc +1 more source

