Clinical data comparison for FDA-approved gene therapies in sickle cell disease. [PDF]
Leonard A, Kanter J.
europepmc +1 more source
Diagnostic Utility of a Multiplex PCR Assay in Detecting Common Mutations of the α-Globin Gene in α-Thalassemia. [PDF]
Park SN, Roh J, Kim JT, Song MJ.
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Structure of the human G gamma-A gamma-delta-beta-globin gene locus.
René Bernards +4 more
openalex +2 more sources
G2B: an optimized lentiviral vector with enhanced titer and β-globin expression for improved β-thalassemia gene therapy. [PDF]
Gao ZY +11 more
europepmc +1 more source
Mechanisms of Globin Gene Regulation in Mammals. [PDF]
Hardison RC.
europepmc +1 more source
Genotype-Phenotype Correlation of Seven Known and Novel β-Globin Gene Variants. [PDF]
Singha K +3 more
europepmc +1 more source
Caught by Whole-Exome Sequencing: Hemoglobin Sun Prairie in a Patient With Unexplained Hemolytic Anemia From Nepal. [PDF]
Upadhaya P, Shrestha A.
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Hematopoietic stem cell therapy with gene modification to treat sickle cell disease. [PDF]
Ball J +4 more
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Molecular identification and phenotypic study of a novel <i>HBB</i>: c.-23A>G mutation in the 5' untranslated region. [PDF]
Shen S +11 more
europepmc +1 more source

