Population Modeling of Factor IX Activity Following Administration of Fidanacogene Elaparvovec Gene Therapy in Participants with Hemophilia B. [PDF]
Wojciechowski J +3 more
europepmc +1 more source
Long-term correction of hemophilia B using adenoviral delivery of CRISPR/Cas9 [PDF]
Curiel, David T +5 more
core +1 more source
Radionuclides in the postoperative management of orthotopic human organ transplantation. [PDF]
Brown, DW, Starzl, TE
core +1 more source
Gene therapy for hemophilia B: results from the phase 1/2 101HEMB01/02 studies. [PDF]
Pipe S +7 more
europepmc +1 more source
Predicting FVIII Activity in Patients Who Use Recombinant FVIII Fc Fusion Protein for Prophylaxis and Treatment of Bleeding Episodes [PDF]
Allen, G +7 more
core
The human genes for hemophilia A and hemophilia B flank the X chromosome fragile site at Xq27.3. [PDF]
Michele Purrello +7 more
openalex +1 more source
Extravascular factor IX after gene therapy in hemophilia B, does it matter? [PDF]
Van Thillo Q, Hermans C.
europepmc +1 more source
Current status of treatment and disease burden of a cohort of hemophilia B in China. [PDF]
Huang Y, Wan C, Guan T, Xi X.
europepmc +1 more source
Completion of phase 2b trial of etranacogene dezaparvovec gene therapy in patients with hemophilia B over 5 years. [PDF]
von Drygalski A +11 more
europepmc +1 more source

