Results 81 to 90 of about 2,581 (157)

Functional, Cohort-Level Assessment of CFTR Modulator Responses Using Biobanked Nasal Epithelial Cells from Individuals with Cystic Fibrosis. [PDF]

J Pers Med
Aalbers BL, Amatngalim GD, Aarts EM, Rodenburg LW, den Hertog-Oosterhoff LA, Heijerman HGM, Beekman JM.   +6 more
europepmc   +1 more source

Lumacaftor inhibits channel activity of rescued F508del cystic fibrosis transmembrane conductance regulator. [PDF]

Am J Physiol Lung Cell Mol Physiol
Ambrosetti AD, Hagedorn ZJ, Bono TR, Wen H, Nguyen R, Rodriguez-Cruz K, Ali J, Palacio H, Phillips AJ, Gilliland SD, Freeman AJ, Thompson J, Fu L, McNicholas CM, Rowe SM, Wang XR.   +15 more
europepmc   +1 more source

Effect of Cystic Fibrosis Transmembrane Conductance Regulator Modulators on Liver Enzymes Among Patients With Cystic Fibrosis: A Systematic Review and Meta-Analysis. [PDF]

Gastro Hep Adv
Vongsavath T, Tun KM, Mukhopadhyay D, Lo CH, Singh A, Amin R, Twohig P, Saab S, Manne V.   +8 more
europepmc   +1 more source

Comparative efficacy and safety of CFTR modulators for people with cystic fibrosis with phe508del mutation: a systematic review and bayesian network meta-analysis. [PDF]

EClinicalMedicine
Safeer V S M, Behl S, Vaidya PC, Tiwari P, Bharti SK, Nahan N, Kumar Sahu J, Bansal D.   +7 more
europepmc   +1 more source

Variation in Use of Lumacaftor/Ivacaftor [PDF]

D37. A PULMONARY AND CRITICAL CARE MEDLEY, 2020
openaire   +1 more source

The effect of elexacaftor-tezacaftor-ivacaftor on liver stiffness in children with cystic fibrosis. [PDF]

J Pediatr Gastroenterol Nutr
Diemer S, Elidottir H, Eklund EA, Påhlman LI, Hansen C.   +4 more
europepmc   +1 more source

Pharmacokinetics of Ivacaftor, Tezacaftor, Elexacaftor, and Lumacaftor in Special Cystic Fibrosis Populations: A Systematic Review. [PDF]

Clin Pharmacokinet
Elzinga FA, Malik PRV, Akkerman OW, Rottier BL, van der Vaart H, Touw DJ, Koppelman GH, Mian P.   +7 more
europepmc   +1 more source

Impact of Elexacaftor/Tezacaftor/Ivacaftor on Fecal Elastase-1 in Children With Cystic Fibrosis. [PDF]

Pediatr Pulmonol
Sankararaman S, Prunty L, Pamer C, Thavamani A, Roesch E, Schindler T.   +5 more
europepmc   +1 more source

Data accuracy in the European Cystic Fibrosis Society Patient Registry: results of an on-site data validation project. [PDF]

Orphanet J Rare Dis
Lutz N, Alice F, Marko K, Nadine W, Mayor SL, Anna Z, Vibha P, ECFS Patient Registry Steering Group.   +7 more
europepmc   +1 more source

Improvement of Cystic Fibrosis-Associated Liver Disease in Adults on Long-Term Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Modulators. [PDF]

Life (Basel)
Manioudaki S, Vasilieva L, Geladari E, Mani I, Athanassa Z, Elefsiniotis I, Hadziyannis E, Sevastianos V, Oikonomou A, Theophilou A, Diamantea F, Alexopoulou A.   +11 more
europepmc   +1 more source