Nuclear receptors in health and disease: signaling pathways, biological functions and pharmaceutical interventions. [PDF]
Jin P+8 more
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Medicines not recommended for inclusion in the who essential medicines list: a retrospective observational study. [PDF]
Costa E+10 more
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Results of health technology assessments of orphan drugs in Germany-lack of added benefit, evidence gaps, and persisting unmet medical needs. [PDF]
Kranz P, McGauran N, Ünal C, Kaiser T.
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Establishment of a value assessment framework for orphan medicinal products in China. [PDF]
Chen H, Xiang Y, Tang X, Hu M.
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Time to consider fracture nonunion an orphan disease? An update into pathophysiology, epidemiology and therapeutic solutions. [PDF]
Vukicevic S+8 more
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Shortage of praziquantel in Europe: a clarion call for urgent action. [PDF]
Lindner AK+10 more
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Navigating health policies and programs in India: exploring opportunities to improve rare disease management and orphan drug research. [PDF]
Mishra S, Bhat D, Venkatesh MP.
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Amelioration of radiation-induced skin injury by tetrahydrobiopterin: preclinical study and phase II trial. [PDF]
Li K, Song B, Yin R, Zhang S.
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Roles of Bile Acid-Activated Receptors in Monocytes-Macrophages and Dendritic Cells. [PDF]
Jia H, He X, Jiang T, Kong F.
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Reforming the innovation system to deliver affordable medicines: a conceptual framework of pharmaceutical innovation as a complex adaptive system (forest) and theory of change. [PDF]
Moon S+4 more
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