Results 131 to 140 of about 15,382 (226)

Efficacy and safety of vemircopan as monotherapy in patients with paroxysmal nocturnal hemoglobinuria. [PDF]

Blood Adv
Kulasekararaj A, Browett P, Risitano AM, Patriquin CJ, Yenerel MN, Marceau D, Sahin F, Algarra JL, Ogawa M, Yu J, Cross NB, Notaro R, Lee JW, Brodsky RA.   +13 more
europepmc   +1 more source

Disease burden and treatment patterns of paroxysmal nocturnal hemoglobinuria in Japan: a real-world survey. [PDF]

Int J Hematol
Sakurai M, Ueda Y, Obara N, Kroes M, Dochi T, Wiyani A, Balp MM, Somenzi O, Taylor Y, Kawaguchi T, Nishimura JI.   +10 more
europepmc   +1 more source

Optimizing Care in Patients with Paroxysmal Nocturnal Hemoglobinuria: Managing Suboptimal Response and Uncontrolled Disease. [PDF]

J Blood Med
Bienz M, Oliver M, Sperlich C, Patriquin CJ.   +3 more
europepmc   +1 more source

Time-Related Burden of Treatment With Parenterally Administered Complement Inhibitors: A Mixed Methods Observational Study Exploring Experiences among Patients With Paroxysmal Nocturnal Hemoglobinuria. [PDF]

Health Sci Rep
Dingli D, Broderick L, Rizio AA, Rucker S, LaGasse K, Carty MK, Burton E, Gordon S, Yen GP, Paulose J, Geevarghese A, Lee S.   +11 more
europepmc   +1 more source

C3 mutations and poor pegcetacoplan response in paroxysmal nocturnal hemoglobinuria. [PDF]

Front Immunol
Rodríguez de Córdoba S, Reparaz Suevos A, González Sanz S, Fernández FJ, Vega MC, Varela EC, Lada Colunga A, Vallejo Llamas JC, Gonzalez-Rodríguez AP.   +8 more
europepmc   +1 more source

Improved Iron Overload with Pegcetacoplan in Eculizumab-Experienced Patients with Paroxysmal Nocturnal Hemoglobinuria. [PDF]

Int J Mol Sci
Shammo J, Hillmen P, Blandino P, Abilash V, Kuter DJ.   +4 more
europepmc   +1 more source

Clinical Profile, Humanistic and Economic Burden of Paroxysmal Nocturnal Hemoglobinuria in Patients Treated With C5 Inhibitors. [PDF]

EJHaem
Gandhi S, Radsak MP, Ueda Y, Balp MM, Wiyani A, Somenzi O, Snellman J, Taylor Y, Simons A, Panse J.   +9 more
europepmc   +1 more source

Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry. [PDF]

Am J Hematol
Röth A, Patriquin CJ, Szer J, Terriou L, Patel AS, Metzger J, Gustovic P, Nishimura JI, Brodsky RA.   +8 more
europepmc   +1 more source

Paroxysmal Nocturnal Hemoglobinuria in a Young Adult Woman: A Representative Case of Recurrent Intravascular Hemolysis. [PDF]

Cureus
Pera R, Lagarteira J, Sá S, Diz R, Gradinaru A.   +4 more
europepmc   +1 more source

Population PK-PD Modeling of Danicopan Add-On Therapy in Participants With Paroxysmal Nocturnal Hemoglobinuria Treated With Ravulizumab or Eculizumab. [PDF]

CPT Pharmacometrics Syst Pharmacol
Chen J, Yang F, Li H, Pradhan R, Ortiz S.   +4 more
europepmc   +1 more source