Unveiling primary Hyperoxaluria type 1: a fortuitous discovery through bone marrow biopsy. [PDF]
Aaboudech TY +6 more
europepmc +1 more source
Cutting through the stones: Unlocking therapeutic potential with gene editing tools for primary hyperoxaluria type 1. [PDF]
Schneller J, Du W, Ding H.
europepmc +1 more source
Efficacy and safety of Oxalobacter formigenes in patients with primary hyperoxaluria: A systematic review and meta-analysis of randomized controlled trials. [PDF]
Khan U +8 more
europepmc +1 more source
Correction: Lumasiran: A Review in Primary Hyperoxaluria Type 1. [PDF]
Kang C.
europepmc +1 more source
Synthesis and hLDHA Inhibitory Activity of New Stiripentol-Related Compounds of Potential Use in Primary Hyperoxaluria. [PDF]
Rico-Molina M +5 more
europepmc +1 more source
Human glyoxylate metabolism revisited: New insights pointing to multi-organ involvement with implications for siRNA-based therapies in primary hyperoxaluria. [PDF]
Wanders RJA +4 more
europepmc +1 more source
Efficient and safe in vivo treatment of primary hyperoxaluria type 1 via LNP-CRISPR-Cas9-mediated glycolate oxidase disruption. [PDF]
Jiang Y +9 more
europepmc +1 more source

