Results 181 to 190 of about 2,156 (206)

Sapropterin to be funded in New Zealand

PharmacoEconomics & Outcomes News, 2018
openaire   +1 more source

Sapropterin treatment of phenylketonuria

2010
openaire   +1 more source

Sapropterin Adjunctive Therapy in PKU

AAP Grand Rounds, 2007
openaire   +1 more source

Triple treatment while trying to conceive with phenylketonuria: A case study on using combined therapies of pegvaliase, sapropterin, and diet

Molecular Genetics and Metabolism
K. O’Bar, L. Wessenberg, S. V. van Calcar, L. Sliwoski   +3 more
semanticscholar   +1 more source

When standard doses fall short: Real-world success with high dose sapropterin in PKU

Molecular Genetics and Metabolism
Christine Horne, A. Tsai, Alexya N. Aguilera, Krista Engen, Shelby Miller, Sarah Krysinski, B. Downey   +6 more
semanticscholar   +1 more source

Long-Term Developmental Progression in Infants and Young Children Taking Sapropterin for Phenylketonuria: A Two-Year Analysis of Safety and Efficacy

Genetics in Medicine, 2015
David Dimmock, Nicola Longo, Sylvia Stockler-Ipsiroglu   +2 more
exaly  

Sepiapterin zeigt signifikante Überlegenheit gegenüber Sapropterin bei Kindern mit PKU

Pädiatrie hands-on
Redaktion Facharztmagazine
semanticscholar   +1 more source

Relative Bioavailability of Sapropterin From Intact and Dissolved Sapropterin Dihydrochloride Tablets and the Effects of Food: A Randomized, Open-Label, Crossover Study in Healthy Adults

Clinical Therapeutics, 2010
exaly  

Sapropterin Therapy Increases Stability of Blood Phenylalanine Levels in Patients With BH4-Responsive Phenylketonuria (PKU)

Molecular Genetics and Metabolism, 2010
Holly LaDuca, Barbara K Burton
exaly  

Resistance training and metabolic control in phenylketonuria: A paradoxical observation in a sapropterin responder.

Medicina clínica (Ed. impresa)
J. Blasco-Alonso, M. García-Ramírez, R. Gil-Gómez   +2 more
semanticscholar   +1 more source