Results 191 to 200 of about 2,156 (206)

Influence of PAH Genotype on Sapropterin Response in PKU: Results of a Single-Center Cohort Study

JIMD Reports, 2013
exaly  

Sapropterin may be beneficial for phenylketonuria

Inpharma Weekly, 2007
openaire   +1 more source

Diet liberalization and health-related quality of life in sepiapterin-treated participants with phenylketonuria who were receiving sapropterin at study entry: Interim results from the phase 3 aphenity extension study

Molecular Genetics and Metabolism
N. Longo, Janet A. Thomas, Melissa Lah, F. Rutsch, L. Guilder, L. Aljouda, A. Burlina, Zhenming Zhao, A. Larkin, K. Ingalls, Catalina Hughes, Neil Smith, A. Muntau   +12 more
semanticscholar   +1 more source

Sapropterin treatment does not enhance the health‐related quality of life of patients with phenylketonuria and their parents

Acta paediatrica, 2017
R. Feldmann, Eva Wolfgart, J. Weglage, F. Rutsch   +3 more
semanticscholar   +1 more source

A Randomized, Placebo-Controlled, Double-Blind Study of Sapropterin to Treat ADHD Symptoms and Executive Function Impairment in Children and Adults With Sapropterin-Responsive Phenylketonuria

Molecular Genetics and Metabolism, 2015
exaly  

Sapropterin Dihydrochloride

openaire   +1 more source

Sapropterin: a guide to its use in hyperphenylalaninaemia

Drugs & Therapy Perspectives, 2009
openaire   +1 more source

Sapropterin improves coronary endothelial function

Inpharma Weekly, 2001
openaire   +1 more source

Sapropterin (Kuvan) for phenylketonuria.

The Medical letter on drugs and therapeutics, 2008
openaire   +1 more source

Sapropterin Hydrochloride Tablets

openaire   +1 more source