Results 131 to 133 of about 669 (133)

Efficacy of Sapropterin Dihydrochloride in Increasing Phenylalanine Tolerance in Children with Phenylketonuria: A Phase III, Randomized, Double-Blind, Placebo-Controlled Study

Journal of Pediatrics, 2009
Nicola Longo, Emil D Kakkis, Dorothy K Grange   +2 more
exaly  

Safety and efficacy of a 22-week treatment with sapropterin dihydrochloride (tetrahydrobiopterin or 6R-BH4) in phenylketonuria (PKU)

2007
F. Feillet, L. Clarcke, P. Lee, J. Bebchuck, C. Meli, J. Bergoffen, A. Dorenbaum, M. Giovannini   +7 more
openaire   +1 more source

Sapropterin dihydrochloride treatment in Turkish patients under four years old with hyperphenylalaninemia

2013
COŞKUN, TURGAY, ÜNAL, ÖZLEM, GÖKMEN ÖZEL, HÜLYA, HİŞMİ, BURCU, DURSUN, ALİ, SİVRİ, HATİCE SERAP, TOKATLI, AYŞEGÜL   +6 more
openaire   +1 more source