Results 151 to 160 of about 270,275 (243)

Correction to 'Integrating transcriptomics and proteomics to assess antisense oligonucleotide safety and efficacy: a time-resolved approach'. [PDF]

NAR Mol Med
europepmc   +1 more source

Antisense oligonucleotide-mediated MDM4 exon 6 skipping impairs tumor growth.

Journal of Clinical Investigation, 2016
M. Dewaele, Tommaso Tabaglio, K. Willekens, M. Bezzi, S. Teo, Diana H. P. Low, Cheryl M. Koh, F. Rambow, M. Fiers, A. Rogiers, E. Radaelli, M. Al-Haddawi, Soo-Yong Tan, Els R. Hermans, F. Amant, Hualong Yan, Manikandan Lakshmanan, Ratnacaram Chandrahaas Koumar, S. Lim, Frederick A. Derheimer, R. Campbell, Zahid Bonday, V. Tergaonkar, M. Shackleton, C. Blattner, J. Marine, E. Guccione   +26 more
semanticscholar   +1 more source

From N-of-1 to versatility in propionic acidemia: Antisense oligonucleotide-mediated skipping of a constitutive <i>PCCA</i> pseudoexon. [PDF]

Mol Ther Nucleic Acids
Totsune E, Wada Y, Mikami-Saito Y, Arai-Ichinoi N, Saijo N, Takayama J, Maeda Y, Nakajima Y, Ohara O, Kure S, Kikuchi A.   +10 more
europepmc   +1 more source

Improved targeted delivery of antisense oligonucleotide with an antibody mask. [PDF]

Nucleic Acids Res
Hsia HE, Zanini C, Simonneau C, Fraidling J, Kraft TE, Mayer K, Sommer A, Indlekofer A, Wirth T, Benz J, Georges G, Langer LM, Gassner C, Larraillet V, Lohmann S, Koller E, Mansø M, Ravn J, Hofer K, Emrich T, Niewöhner J, Schumacher F, Brinkmann U.   +22 more
europepmc   +1 more source

FACS-based dual fluorescence reporter assay demonstrates efficacy of antisense oligonucleotide therapy of novel <i>PRPF3</i> intronic splice variant. [PDF]

Mol Ther Nucleic Acids
Dolgin V, Eremenko E, Narkis G, Mazor-Oring M, Gradstein L, Birk OS.   +5 more
europepmc   +1 more source

Nanocarriers of Antisense Oligonucleotides in Diabetes [PDF]

, 2012
Rapini, N, BOTTINI, NUNZIO, BOTTINI, MASSIMO   +2 more
openaire   +2 more sources

Mongersen, an oral SMAD7 antisense oligonucleotide, and Crohn's disease.

New England Journal of Medicine, 2015
G. Monteleone, M. Neurath, S. Ardizzone, A. Di Sabatino, M. Fantini, F. Castiglione, M. Scribano, A. Armuzzi, F. Caprioli, G. Sturniolo, F. Rogai, M. Vecchi, R. Atreya, F. Bossa, S. Onali, M. Fichera, G. Corazza, L. Biancone, V. Savarino, R. Pica, A. Orlando, F. Pallone   +21 more
semanticscholar   +1 more source

Antisense Oligonucleotide Therapy for Amyotrophic Lateral Sclerosis (ALS): An Umbrella Review. [PDF]

Cureus
Jeong E, Li D.
europepmc   +1 more source

Glycogen for Smyd3-antisense oligonucleotide delivery and enhanced liver cancer gene therapy. [PDF]

RSC Adv
Bai N, Huang Y, Shen J, Peng Y, Zhang H, Hou D.   +5 more
europepmc   +1 more source