Results 71 to 80 of about 6,602 (127)

呼吸器症状を示すフトアゴヒゲトカゲの病原体解析に関する研究 [PDF]

open access: yes
岐阜大学(Gifu University)博士(獣医学)博士論文 (Doctoral dissertation)doctoral ...
赤羽, 良仁
core  

First-in-human study of TN-201, an AAV9 gene replacement therapy in MYBPC3-associated hypertrophic cardiomyopathy: initial safety, pharmacodynamic, and imaging results from MyPEAK-1. [PDF]

open access: yesCardiovasc Res
Desai MY   +17 more
europepmc   +1 more source

A Rationally Designed AAV9-DM Capsid with Minimal Liver Tropism. [PDF]

open access: yesCells
Nabakowski ZC   +3 more
europepmc   +1 more source

The Impact of QSP Modeling on the Design and Optimization of Gene Therapy Approaches. [PDF]

open access: yesCPT Pharmacometrics Syst Pharmacol
Rayad N, Chowdhury EA, Meno-Tetang GML.
europepmc   +1 more source

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