呼吸器症状を示すフトアゴヒゲトカゲの病原体解析に関する研究 [PDF]
岐阜大学(Gifu University)博士(獣医学)博士論文 (Doctoral dissertation)doctoral ...
赤羽, 良仁
core
First-in-human study of TN-201, an AAV9 gene replacement therapy in MYBPC3-associated hypertrophic cardiomyopathy: initial safety, pharmacodynamic, and imaging results from MyPEAK-1. [PDF]
Desai MY +17 more
europepmc +1 more source
Mosaic AAV mediates efficient transduction across the central and peripheral nervous systems. [PDF]
Jiang M +5 more
europepmc +1 more source
A Rationally Designed AAV9-DM Capsid with Minimal Liver Tropism. [PDF]
Nabakowski ZC +3 more
europepmc +1 more source
Pervasive horizontal transfer of adeno-associated virus capsid genes. [PDF]
Gifford RJ.
europepmc +1 more source
Compact Calm1 promoter enables AAV mediated neuron-targeted expression in human iPSC-derived brain organoids. [PDF]
Klockner I +4 more
europepmc +1 more source
The Impact of QSP Modeling on the Design and Optimization of Gene Therapy Approaches. [PDF]
Rayad N, Chowdhury EA, Meno-Tetang GML.
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Development of human gene reporter cell lines using rAAV mediated homologous recombination [PDF]
core +1 more source

