Results 191 to 200 of about 29,161 (207)

Becker muscular dystrophy patients with deletions around exon 51; a promising outlook for exon skipping therapy in Duchenne patients

Neuromuscular Disorders, 2010
Bert Bakker, Jan Verschuuren, Annemieke Aartsma-Rus   +2 more
exaly  

Exon skipping for dysferlinopathies

2012
Aartsma-Rus, A., Verwey, N., Schneiderat, P., Maarel, S.M. van der, Ommen, G.J.B. van, Houweling-Gazzoli, I.   +5 more
openaire   +1 more source

Antisense‐mediated exon skipping: a therapeutic strategy for titin‐based dilated cardiomyopathy

EMBO Molecular Medicine, 2015
, Alessandra Moretti, Marta Murgia
exaly  

Exon skipping-mediated dystrophin reading frame restoration for small mutations

Human Mutation, 2009
Daniela Perrone, Alessandra Ferlini, Francesca Gualandi   +2 more
exaly  

Multiple exon skipping compositions for DMD

2010
SAZANI PETER, KOLE RYSZARD
openaire   +14 more sources

MEANS AND METHOD FOR INDUCING EXON-SKIPPING

2007
AARTSMA-RUS ANNEMIEKE, VAN DEUTEKOM JUDITH CHRISTINA THEODORA, VAN OMMEN GARRIT-JAN BOUDEWIJN   +2 more
openaire   +5 more sources

Exon Skipping and Inclusion Therapies

2018
openaire   +1 more source

Exon skipping therapy for DMD.

Journal of neuromuscular diseases, 2022
openaire   +1 more source

Exon-skipping therapy for Duchenne muscular dystrophy

The Lancet, 2012
openaire   +2 more sources

DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES

2023
FROELICH STEVEN MICHAEL, WOLOSZYNEK JOSH, MAGAT JENNA-MARIE, VAN DEUTEKOM JUDITH CHRISTINA THEODORA, DE VISSER PETER CHRISTIAN, DATSON NICOLE ANN   +5 more
openaire   +1 more source