Gene therapy for hemoglobinopathies: Clinical trial results and biology of hematopoietic stem cell and the bone marrow niche. [PDF]
Aprile A, Lidonnici MR, Ferrari G.
europepmc +1 more source
The Masked Thalassemia: A Rare Case of a Patient with Normal HbA2 Levels, β-Thalassemia Pathogenic Variant (CD39 C>T), and a Novel δ-Globin Gene Deletion. [PDF]
Chetta M +10 more
europepmc +1 more source
Globin synthesis in fractionated Normoblasts of beta-thalassemia heterozygotes. [PDF]
W. G. Wood, G Stamatoyannopoulos
openalex +1 more source
Comprehensive regulation of γ-globin expression by epigenetic modifications and protein post-translational modifications. [PDF]
Ye D +5 more
europepmc +1 more source
Transfer of human globin genes to erythroleukemic mouse cells. [PDF]
Demetrios�� Spandidos, John Paul
openalex +1 more source
Analysis of Hematological Parameters in Relation to Genotypes in 497 Patients with Hemoglobin H Disease. [PDF]
Lan L, Zheng Z, Wu H.
europepmc +1 more source
A Novel Mutation in the α2-Globin Gene in Two Unrelated Iranian Families
Tayebeh Hamzehloei +2 more
openalex +2 more sources
Ex Vivo Gene and Cell Therapy in Hematopoietic Stem Cells. [PDF]
Petrova IO, Smirnikhina SA.
europepmc +1 more source
Isolation and characterization of recombinant clones containing the chicken adult beta-globin gene.
Gordon D. Ginder +2 more
openalex +1 more source
Triple base editor catalyzes saturation mutation of adenine, cytidine, and guanine. [PDF]
Wu Y +10 more
europepmc +1 more source

