Results 191 to 200 of about 72,117 (254)

From N-of-1 to versatility in propionic acidemia: Antisense oligonucleotide-mediated skipping of a constitutive <i>PCCA</i> pseudoexon. [PDF]

open access: yesMol Ther Nucleic Acids
Totsune E   +10 more
europepmc   +1 more source

Targeting TLK2 with antisense oligonucleotides as a new strategy in acute myeloid leukemia. [PDF]

open access: yesFront Oncol
Lin HY   +9 more
europepmc   +1 more source

RNA-based precision medicine in glioblastoma driven by oncogenic gene fusions. [PDF]

open access: yesMol Ther Oncol
Bouillon M   +6 more
europepmc   +1 more source

Poster Sessions

open access: yes
HemaSphere, Volume 10, Issue S1, June 2026.
wiley   +1 more source

Publication Only

open access: yes
HemaSphere, Volume 10, Issue S1, June 2026.
wiley   +1 more source

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