Results 41 to 50 of about 722,064 (339)

Data from the US and UK cystic fibrosis registries support disease modification by CFTR modulation with ivacaftor

Thorax, 2018
Background Ivacaftor is the first cystic fibrosis transmembrane conductance regulator (CFTR) modulator demonstrating clinical benefit in patients with cystic fibrosis (CF).
L. Bessonova, N. Volkova, M. Higgins, L. Bengtsson, S. Tian, C. Simard, M. Konstan, G. Sawicki, A. Sewall, S. Nyangoma, A. Elbert, B. Marshall, D. Bilton   +12 more
semanticscholar   +1 more source

Relation of Adverse Childhood Experiences to Clinical and Patient‐Reported Outcomes for Adults With Sickle Cell Disease: A Registry Study

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Background Adverse childhood experiences (ACEs) are stressful or traumatic events prior to age 18 that are known to have a lasting impact on individuals’ health and well‐being. There is a gap in understanding the relationship between ACEs and Other Life Stressors and health status for adults with sickle cell disease (SCD).
Marsha Treadwell, Jessica Liang, Liliana Preiss, Angela Rivers, Jane S. Hankins, Allison King, Justin Williams, Michael B. Potter, Danielle Hessler   +8 more
wiley   +1 more source

Achieving Thoracic Oncology data collection in Europe: a precursor study in 35 Countries [PDF]

, 2018
Background: A minority of European countries have participated in international comparisons with high level data on lung cancer. However, the nature and extent of data collection across the continent is simply unknown, and without accurate data ...
Alfageme Michavila, Inmaculada, Baldwin, David, Beckett, Paul, Berghmans, Thierry, Brincat, Stephen, Burghuber, Otto, Corlateanu, Alexandru, Rich, Anna   +7 more
core   +1 more source

Oral cancer statistics in India on the basis of first report of 29 population-based cancer registries

Journal of Oral and Maxillofacial Pathology, 2018
Objectives: To summarize and provide an overview of age-specific oral cancer incidence reported in 29 population-based cancer registry in India. Materials and Methods: Secondary data on age-adjusted rates (AARs) of incidence of oral cancer and other ...
Swati Sharma, L. Satyanarayana, S. Asthana, KK Shivalingesh, B. Goutham, S. Ramachandra   +5 more
semanticscholar   +1 more source

What to Do When Medical Evidence Can Only Be Generated Through Routine Data: An Example From Pediatric Oncology

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Children undergoing allogeneic stem cell transplantation often receive off‐label rituximab treatment for Epstein–Barr virus reactivation, using adult dosing without pediatric evidence. This project aims to develop a clinical decision support tool (CDSS) that provides evidence‐based dosing scenarios by analyzing real‐world patient data.
Birgit Burkhardt, Antje Walz, Dietrich Knoerzer   +2 more
wiley   +1 more source

Non-vitamin K Antagonist Oral Anticoagulant, Warfarin, and ABC Pathway Adherence on Hierarchical Outcomes: Win Ratio Analysis of the COOL-AF Registry [PDF]

, 2023
Sukrit Treewaree, Gregory Y.H. Lip, Rungroj Krittayaphong   +2 more
openalex   +1 more source

The MedSupport Multilevel Intervention to Enhance Support for Pediatric Medication Adherence: Development and Feasibility Testing

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Introduction We developed MedSupport, a multilevel medication adherence intervention designed to address root barriers to medication adherence. This study sought to explore the feasibility and acceptability of the MedSupport intervention strategies to support a future full‐scale randomized controlled trial.
Elizabeth G. Bouchard, Hital Patel, Paula C. Vincent, Justine Kahn, Kira Bona, Thai Hoa Tran, Elisa M. Rodriguez, Kristopher Attwood, Kara M. Kelly   +8 more
wiley   +1 more source

The relevance of EU directive 2010/53/EU for living organ donation practice [PDF]

, 2016
With the recent transposition of Directive 2010/53/EU into the transplant regulation of EU Member States, the time is right to have a closer look at its implications for living organ donation practice.
Burnapp, Lisa, Citterio, Franco, Dor, Frank, Frunza, Mihaela, Johnson, Rachel, Lennerling, Annette, Mamode, Nizam, Sterckx, Sigrid, Van Assche, Kristof, Weimar, Willem, Zuidema, Willij   +10 more
core   +1 more source

9‐Year Trend in the Management of Acute Heart Failure in Japan: A Report From the National Consortium of Acute Heart Failure Registries

Journal of the American Heart Association : Cardiovascular and Cerebrovascular Disease, 2018
Background Acute heart failure (AHF) is a heterogeneous condition, and its characteristics and management patterns differ by region. Furthermore, limited evidence is available on AHF outside of Western countries.
Y. Shiraishi, S. Kohsaka, N. Sato, T. Takano, T. Kitai, T. Yoshikawa, Y. Matsue   +6 more
semanticscholar   +1 more source

Stereotactic Body Radiation Therapy for Pediatric, Adolescent, and Young Adult Patients With Osteosarcoma: Local Control Outcomes With Dosimetric Analysis

Pediatric Blood &Cancer, EarlyView.
ABSTRACT Background/Objectives Osteosarcoma is a radioresistant tumor that may benefit from stereotactic body radiation therapy (SBRT) for locoregional control in metastatic/recurrent disease. We report institutional practice patterns, outcomes, toxicity, and failures in osteosarcoma patients treated with SBRT.
Jenna Kocsis, Shauna R. Campbell, Jonathan Jang, Eashwar Somasundaram, Chandana A. Reddy, Jacob G. Scott, Lilyana Angelov, Peter M. Anderson, Matteo Trucco, Zachary Burke, Lukas Nystrom, Nathan Mesko, Anthony Magnelli, Erin S. Murphy   +13 more
wiley   +1 more source