Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping [PDF]
, 2012 Aurélie Goyenvalle +6 more
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Dystrophin-deficiency stiffens skeletal muscle and impairs elasticity: an in vivo rheological examination [PDF]
Pavithran Devananthan +6 more
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Impact of dystrophin deficiency on vascular smooth muscle cell. [PDF]
Sci RepXuan W +4 more
europepmc +1 more source
Dystrophin protects the sarcolemma from stresses developed during muscle contraction.
, 1993 Basil J. Petrof +4 more
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623. Dystrophin Exon 52-Deleted Pigs as a New Animal Model of Duchenne Muscular Dystrophy: Its Characterization and Potential as a Tool for Developing Exon Skipping Therapy [PDF]
, 2016 Yusuke Echigoya +8 more
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Dystrophin Restorative and Compensatory Gene Addition Therapies for Duchenne Muscular Dystrophy: Could CRISPRa Provide a Realistic Alternative? [PDF]
MusclesRostamitehrani Z, Javed R, Popplewell L.
europepmc +1 more source
Defects in neuromuscular junction structure in dystrophic muscle are corrected by expression of a NOS transgene in dystrophin-deficient muscles, but not in muscles lacking - and 1-syntrophins [PDF]
, 2004 T. Shiao
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Genetic strategies for therapy of Duchenne muscular dystrophy. [PDF]
Mol Ther Nucleic AcidsŁoboda A, Chamberlain JS, Dulak J.
europepmc +1 more source