Results 131 to 140 of about 23,636 (243)

PITX2 Enhances the Regenerative Potential of Dystrophic Skeletal Muscle Stem Cells

open access: yesStem Cell Reports, 2018
Summary: Duchenne muscular dystrophy (DMD), one of the most lethal genetic disorders, involves progressive muscle degeneration resulting from the absence of DYSTROPHIN.
Daniel Vallejo   +7 more
doaj  

Deletions in the 5' region of dystrophin and resulting phenotypes.

open access: green, 1994
Francesco Muntoni   +9 more
openalex   +1 more source

Systemic Antisense Therapeutics for Dystrophin and Myostatin Exon Splice Modulation Improve Muscle Pathology of Adult mdx Mice

open access: yesMolecular Therapy: Nucleic Acids, 2017
Antisense-mediated exon skipping is a promising approach for the treatment of Duchenne muscular dystrophy (DMD), a rare life-threatening genetic disease due to dystrophin deficiency.
Ngoc Lu-Nguyen   +5 more
doaj  

G-utrophin, the autosomal homologue of dystrophin Dp116, is expressed in sensory ganglia and brain. [PDF]

open access: green, 1995
Derek J. Blake   +7 more
openalex   +1 more source

Herpes simplex virus vector-mediated dystrophin gene transfer and expression in MDX mouse skeletal muscle [PDF]

open access: bronze, 1999
Giridhar R. Akkaraju   +7 more
openalex   +1 more source

The role of dystrophin isoforms and interactors in the brain. [PDF]

open access: yesBrain
Tetorou K   +4 more
europepmc   +1 more source

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