Results 161 to 170 of about 48,181 (245)

DMD carrier model with mosaic dystrophin expression in the heart reveals complex vulnerability to myocardial injury

, 2020
Tatyana A. Meyers, Jackie A. Heitzman, DeWayne Townsend   +2 more
openalex   +2 more sources

Specificity and VH sequence of two monoclonal antibodies against the N-terminus of dystrophin [PDF]

, 1995
Glenn E. Morris, Serge Muyldermans, Nguyen thi Mân   +2 more
openalex   +1 more source

Dystrophin Restorative and Compensatory Gene Addition Therapies for Duchenne Muscular Dystrophy: Could CRISPRa Provide a Realistic Alternative? [PDF]

Muscles
Rostamitehrani Z, Javed R, Popplewell L.
europepmc   +1 more source

Genetic strategies for therapy of Duchenne muscular dystrophy. [PDF]

Mol Ther Nucleic Acids
Łoboda A, Chamberlain JS, Dulak J.
europepmc   +1 more source

Destabilization of the Dystrophin-Glycoprotein Complex without Functional Deficits in α-Dystrobrevin Null Muscle

, 2008
Tina M. Bunnell, Michele A. Jaeger, Daniel P. Fitzsimons, Kurt W. Prins, James M. Ervasti   +4 more
openalex   +2 more sources

Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy [PDF]

, 2018
Dongsheng Duan
openalex   +1 more source

A review of recent studies on CRISPR/Cas9-mediated genome editing in a variety of muscle-related genetic disorders. [PDF]

J Transl Med
Lyu G, Li P, Lang W.
europepmc   +1 more source

A Comparative Study of N-glycolylneuraminic Acid (Neu5Gc) and Cytotoxic T Cell (CT) Carbohydrate Expression in Normal and Dystrophin-Deficient Dog and Human Skeletal Muscle

, 2014
Paul T. Martin, Bethannie Golden, Jonathan Okerblom, Marybeth Camboni, Kumaran Chandrasekharan, Rui Xu, Ajit Varki, Kevin M. Flanigan, Joe N. Kornegay   +8 more
openalex   +2 more sources

Clinical and molecular characterization of a cohort of patients with novel nucleotide alterations of the Dystrophin gene detected by direct sequencing [PDF]

, 2011
Francesca Magri, Roberto Del Bo, Maria Grazia D’Angelo, Alessandra Govoni, Serena Ghezzi, S. Gandossini, Monica Sciacco, Patrizia Ciscato, Andreina Bordoni, Silvana Tedeschi, Francesco Fortunato, Valeria Lucchini, Matteo Cereda, Stefania Corti, Maurizio Moggio, Nereo Bresolin, Giacomo P. Comi   +16 more
openalex   +1 more source

Intrinsic dysfunction in muscle stem cells lacking dystrophin begins during secondary myogenesis. [PDF]

Nat Commun
Esper ME, Lin AYT, Bennett D, Rudnicki MA.   +3 more
europepmc   +1 more source