Results 181 to 190 of about 160,917 (252)

Targeting the Roots of Kidney Disease: Systematic Review of the Therapies Targeting the Complement System. [PDF]

Medicina (Kaunas)
Roman M, Nowicki M.
europepmc   +1 more source

First insights into the genetic composition of <i>M. tuberculosis</i> population circulating in Kosovo. [PDF]

J Clin Tuberc Other Mycobact Dis
Minias A, Kuzioła M, Ahmeti F, Mehmeti N, Jerliu B, Lila G, Miftari A, Shkodra X, Jakupi X, Kacaniku Z, Kozińska M, Zabost A, Słomka M, Strapagiel D, Dziadek J, Augustynowicz-Kopeć E, Bajrami R.   +16 more
europepmc   +1 more source

Global insight into rare disease and orphan drug definitions: a systematic literature review. [PDF]

BMJ Open
Abozaid GM, Kerr K, Alomary H, Al-Omar HA, McKnight A.   +4 more
europepmc   +1 more source

Unlocking the Mysteries of Rare Disease Drug Development: A Beginner's Guide for Clinical Pharmacologists. [PDF]

Clin Transl Sci
Ahmed MA, AbuAsal B, Barrett JS, Azer K, Hon YY, Albusaysi S, Shang E, Wang M, Burian M, Rayad N.   +9 more
europepmc   +1 more source

OVERVIEW OF REGULATORY INITIATIVES IN THE EUROPEAN UNION TO STIMULATE RESEARCH AND ACCELERATE ACCESS TO ORPHAN DRUGS AND OTHER HIGH MEDICAL NEED PRODUCTS

Acta Poloniae Pharmaceutica - Drug Research, 2019
Marcin Czech, Coen Kooiker, Aleksandra Baran-Kooiker   +2 more
openaire   +2 more sources

The Orphan Receptor GPR151: Discovery, Expression, and Emerging Biological Significance. [PDF]

ACS Chem Neurosci
DePasquale O, O'Brien C, Gordon B, Barker DJ.   +3 more
europepmc   +1 more source

ROR1 as an Immunotherapeutic Target for Inducing Antitumor Helper T Cell Responses Against Head and Neck Squamous Cell Carcinoma. [PDF]

Cancers (Basel)
Sato R, Yamaki H, Inoue T, Sakaue S, Ominato H, Wakisaka R, Komatsuda H, Kono M, Ohara K, Kosaka A, Ohkuri T, Nagato T, Kumai T, Kishibe K, Kobayashi H, Takahara M.   +15 more
europepmc   +1 more source

Towards a sustainable rare disease and orphan drug ecosystem in Saudi Arabia: policy insights from a multi-stakeholder workshop. [PDF]

Front Pharmacol
Abozaid GM, Al-Omar HA, Alrabiah A, AlMuaither A, McKnight AJ.   +4 more
europepmc   +1 more source

The impact of rare diseases on the quality of life in paediatric patients: current status. [PDF]

Front Public Health
Dumbuya JS, Zeng C, Deng L, Li Y, Chen X, Ahmad B, Lu J.   +6 more
europepmc   +1 more source

Expediting treatments in the 21st century: orphan drugs and accelerated approvals. [PDF]

Orphanet J Rare Dis
Domike R, Raju GK, Sullivan J, Kennedy A.   +3 more
europepmc   +1 more source