Decoding the structure and translational promise of ROOL RNA nanocages. [PDF]
Lou H, Ding Y, Duan S.
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Emerging Gene Therapies in Sickle Cell Disease: A Comparative Review of Efficacy and Safety Against Standard Treatments. [PDF]
Kabrah SM.
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Using modified mRNA for cardiomyocyte proliferation and cardiac genetic disease modelling and treatment. [PDF]
Batho CAP, Hudson JE, Wilson CH.
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Gene therapy for disorders of sex development: current applications and future challenges. [PDF]
Peng W, Zhao Q, Chen J, Peng H, Jiang H.
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Gene Therapy for Inherited Retinal Disease: Current Strategies, Personalized Medicine, and Future Implications-A Comprehensive Review. [PDF]
Butt FR +8 more
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Ex Vivo Gene and Cell Therapy in Hematopoietic Stem Cells. [PDF]
Petrova IO, Smirnikhina SA.
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Seamless and Highly Efficient Site-directed Mutagenesis for Protein, RNA, and Plasmid Engineering. [PDF]
Yang XJ.
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Impairment of the Uroporphyrinogen Decarboxylase 2 Gene Induces Lesion Mimicry and Downregulates Tetrapyrrole Biosynthesis Pathway Genes in Rice. [PDF]
Qu M +12 more
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Harnessing the potential of gene editing technology for CAR-T cell therapy of solid tumors. [PDF]
Khodabandehloo E +5 more
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